Award
National Institute of Neurological Disorders and Stroke 5R01NS135254-03
Alternative Splicing and Development of Small Molecule Therapeutics in CAG Expansion Spinocerebellar Ataxias
Recipient
State University of New York at Albany
Award Amount
$570,215.00
Ceiling
$570,215.00
Awarded
December 30, 2025
Identifier
5R01NS135254-03
NIH-funded research project at State University of New York at Albany to develop small molecule therapeutics for spinocerebellar ataxias by studying alternative splicing and CAG expansions.
Description
Research project focusing on spinocerebellar ataxias (SCAs), exploring therapeutic potential of small molecules targeting CAG expansions, involving transcriptomic analysis, alternative splicing, and development of therapeutic compounds.