Award
National Center for Advancing Translational Sciences 1R21TR005475-01
Optimization and Preclinical Validation of QTE Therapy for Friedreich's Ataxia
Recipient
University of Florida, Gainesville, FL
Award Amount
$419,375.00
Ceiling
$419,375.00
Awarded
July 07, 2025
Identifier
1R21TR005475-01
The award supports the optimization and preclinical validation of QTE therapy for Friedreich's Ataxia, focusing on dosage and formulation improvements and preparing for clinical trials to provide a safer, more effective treatment.
Description
This project aims to optimize dosage and formulation of QTE therapy for Friedreich's Ataxia, with plans to transition from preclinical to clinical trials, leveraging orphan drug benefits and community engagement strategies.