Award
Children's Hospital of Philadelphia 1R21TR006299-01A1
Patient-Centric Clinical Outcome Measures for Multiple Sulfatase Deficiency (MSD)
Recipient
Children's Hospital of Philadelphia, Philadelphia, PA, United States
Award Amount
$489,500.00
Ceiling
$489,500.00
Awarded
September 03, 2025
Identifier
1R21TR006299-01A1
NIH grant awarded to develop patient-centric clinical outcome measures for Multiple Sulfatase Deficiency with a budget of $489,500 from 2025 to 2027.
Description
This is a NIH grant project focusing on developing patient-centric outcome measures for MSD, with a budget of $489,500, spanning from September 2025 to September 2027. The project involves natural history studies, validation of assessment tools, and will support future clinical trials targeting MSD.