Award
National Center for Advancing Translational Sciences 1R21TR005475-01
Optimization and Preclinical Validation of QTE Therapy for Friedreich's Ataxia
Recipient
University of Florida
Award Amount
$419,375.00
Ceiling
$419,375.00
Awarded
July 07, 2025
Identifier
1R21TR005475-01
Award for optimizing and validating QTE therapy for Friedreich's Ataxia, including preclinical studies and preparation for clinical trials.
Description
This NIH SBIR/STTR grant aims to optimize and validate a novel QTE therapy for Friedreich's Ataxia, focusing on dosage, formulation, and efficacy in preclinical models, with plans for clinical trial transition and community engagement.