# NIH Reporter #1R21TR006299-01A1

Patient-Centric Clinical Outcome Measures for Multiple Sulfatase Deficiency (MSD)

**Recipient:** Children's Hospital of Philadelphia

**Award Amount:** $489,500.00
**Ceiling:** $489,500.00

**Awarded:** September 03, 2025

**Identifier:** 1R21TR006299-01A1

The National Center for Advancing Translational Sciences funded a two-year project at Children's Hospital of Philadelphia to evaluate patient- and clinician-reported outcome measures for Multiple Sulfatase Deficiency and help prepare for future clinical trials.

### Description

Project to develop and validate patient-centric and clinical outcome measures for Multiple Sulfatase Deficiency, supporting disease progression assessment and future clinical trials.

[View original record](https://reporter.nih.gov/search/O7rUSzRdDUaj-f_y7VGw-A/project-details/11088079)